CanadaA unique company
dedicated to improving the health and quality of life of Americans with rare diseases by making orphan drugs available in the U.S.
What is a rare disease?
An illness that affects fewer than 200,000 Americans at any given time, thereby limiting scientific research, clinical expertise and patient access to effective treatment options
What is an orphan drug?
A medication or other medicinal product used to treat a rare disease or disorder
This site is intended for US residents only. Medical practices, products and/or regulations can be different from one country to another and as a result, the medical and/or product information on this site is not appropriate for use outside of the United States. The information is not meant to suggest any medical course of action. Rather, it is intended to inform and to raise awareness so that these issues can be discussed with qualified Healthcare Professionals.